Featured
-
-
Article
| Open AccessMetabolic flux profiling of MDCK cells during growth and canine adenovirus vector production
- Nuno Carinhas
- , Daniel A. M. Pais
- & Ana P. Teixeira
-
Article
| Open AccessMinicircle DNA Provides Enhanced and Prolonged Transgene Expression Following Airway Gene Transfer
- Mustafa M. Munye
- , Aristides D. Tagalakis
- & Stephen L. Hart
-
Article
| Open AccessAAV Gene Therapy for MPS1-associated Corneal Blindness
- Melisa Vance
- , Telmo Llanga
- & Matthew L. Hirsch
-
Article
| Open AccessEnhanced renoprotective effect of IGF-1 modified human umbilical cord-derived mesenchymal stem cells on gentamicin-induced acute kidney injury
- Pengfei Liu
- , Yetong Feng
- & Yulai Zhou
-
Article
| Open AccessNF-κB promotes leaky expression of adenovirus genes in a replication-incompetent adenovirus vector
- M. Machitani
- , F. Sakurai
- & H. Mizuguchi
-
Article
| Open AccessIn situ genetic correction of F8 intron 22 inversion in hemophilia A patient-specific iPSCs
- Yong Wu
- , Zhiqing Hu
- & Desheng Liang
-
Article
| Open AccessHIV-1 CCR5 gene therapy will fail unless it is combined with a suicide gene
- Aridaman Pandit
- & Rob J. de Boer
-
Article
| Open AccessAn Autogenously Regulated Expression System for Gene Therapeutic Ocular Applications
- Matthew A. Sochor
- , Vidyullatha Vasireddy
- & Mitchell Lewis
-
Article
| Open AccessAntitumor potential of a synthetic interferon-alpha/PLGF-2 positive charge peptide hybrid molecule in pancreatic cancer cells
- Hongmei Yin
- , Naifei Chen
- & Ji-Fan Hu
-
Article
| Open AccessControlled delivery of β-globin-targeting TALENs and CRISPR/Cas9 into mammalian cells for genome editing using microinjection
- Renee N. Cottle
- , Ciaran M. Lee
- & Gang Bao
-
Article
| Open AccessMessenger RNA-based therapeutics for the treatment of apoptosis-associated diseases
- Akitsugu Matsui
- , Satoshi Uchida
- & Kazunori Kataoka
-
Article
| Open AccessGenome editing of CXCR4 by CRISPR/cas9 confers cells resistant to HIV-1 infection
- Panpan Hou
- , Shuliang Chen
- & Deyin Guo
-
Article
| Open AccessCombinatorial RNA Interference Therapy Prevents Selection of Pre-existing HBV Variants in Human Liver Chimeric Mice
- Yao-Ming Shih
- , Cheng-Pu Sun
- & Mi-Hua Tao
-
Article
| Open AccessAn optimized method for high-titer lentivirus preparations without ultracentrifugation
- Wei Jiang
- , Rui Hua
- & Chen Zhang
-
Article
| Open AccessBoth TALENs and CRISPR/Cas9 directly target the HBB IVS2–654 (C > T) mutation in β-thalassemia-derived iPSCs
- Peng Xu
- , Ying Tong
- & De-pei Liu
-
Article
| Open AccessFoxO1-negative cells are cancer stem-like cells in pancreatic ductal adenocarcinoma
- Weifeng Song
- , Qi Li
- & Liwei Wang
-
Article
| Open AccessClathrin inhibitor Pitstop-2 disrupts the nuclear pore complex permeability barrier
- Ivan Liashkovich
- , Dzmitry Pasrednik
- & Victor Shahin
-
Article
| Open AccessCanine helper-dependent vectors production: implications of Cre activity and co-infection on adenovirus propagation
- Paulo Fernandes
- , Ana I. Almeida
- & Ana S. Coroadinha
-
Article
| Open AccessConstruction of stable packaging cell lines for clinical lentiviral vector production
- Khaled S. Sanber
- , Sean B. Knight
- & Yasuhiro Takeuchi
-
Article
| Open AccesssiRNAs targeted to Smad4 prevent renal fibrosis in vivo
- Yoshiyuki Morishita
- , Hiromichi Yoshizawa
- & Daisuke Nagata
-
Article
| Open AccessNovel lentiviral vectors with mutated reverse transcriptase for mRNA delivery of TALE nucleases
- Ulrike Mock
- , Kristoffer Riecken
- & Boris Fehse
-
Article
| Open AccessTranscription activator-like effector nuclease-mediated transduction of exogenous gene into IL2RG locus
- Yohei Matsubara
- , Tomoki Chiba
- & Hiroshi Asahara
-
Article
| Open AccessNon-integrating gamma-retroviral vectors as a versatile tool for transient zinc-finger nuclease delivery
- Sylwia Bobis-Wozowicz
- , Melanie Galla
- & Toni Cathomen
-
Article
| Open AccessSystemic delivery of miR-126 by miRNA-loaded Bubble liposomes for the treatment of hindlimb ischemia
- Yoko Endo-Takahashi
- , Yoichi Negishi
- & Yukihiko Aramaki
-
Article
| Open AccessModular adeno-associated virus (rAAV) vectors used for cellular virus-directed enzyme prodrug therapy
- Sven Hagen
- , Tobias Baumann
- & Kristian M. Müller
-
Article
| Open AccessAdenovirus vectors lacking virus-associated RNA expression enhance shRNA activity to suppress hepatitis C virus replication
- Zheng Pei
- , Guoli Shi
- & Yumi Kanegae
-
Article
| Open AccessDevelopment of novel DNA vaccine for VEGF in murine cancer model
- Mariko Kyutoku
- , Hironori Nakagami
- & Ryuichi Morishita
-
Article
| Open AccessExpanded activity of dimer nucleases by combining ZFN and TALEN for genome editing
- Wei Yan
- , Cory Smith
- & Linzhao Cheng
-
Article
| Open AccessEfficient production of adenovirus vector lacking genes of virus-associated RNAs that disturb cellular RNAi machinery
- Aya Maekawa
- , Zheng Pei
- & Yumi Kanegae
-
Article
| Open AccessEffect of rapamycin on immunity induced by vector-mediated dystrophin expression in mdx skeletal muscle
- Saman Eghtesad
- , Siddharth Jhunjhunwala
- & Paula R. Clemens
-
Article
| Open AccessTherapeutic potential of HIV protease-activable CASP3
- Kosuke Miyauchi
- , Emiko Urano
- & Jun Komano